Posts by: Marta Figueiredo

Marta Figueiredo

Marta Figueiredo holds a BSc in Biology and a MSc in Evolutionary and Developmental Biology from the University of Lisbon, Portugal. She is currently finishing her PhD in Biomedical Sciences at the University of Lisbon, where she focused her research on the role of several signalling pathways in thymus and parathyroid glands embryonic development.

November 6, 2019November 6, 2019

BioMarin Submits Clinical Trial Application to Evaluate BMN 307 Gene Therapy in UK Phenylketonuria Patients

News

BioMarin Pharmaceutical has submitted a clinical trial application (CTA) to the U.K.’s Medicines and Healthcare products Regulatory Agency (MHRA) to evaluate BMN 307 — its first investigational gene therapy for phenylketonuria (PKU) — ... Read more

October 30, 2019October 30, 2019

Genetic Treatments Showing Promise, Homology Announces; Trial Underway in Adults with PKU

News

Homology Medicines’ candidate treatments in gene editing and gene therapy significantly reduced phenylalanine levels — which are dangerously high in people with phenylketonuria (PKU) — in a mouse model of the disease, the ... Read more